It’s been a year since the gene-editing treatment Casgevy was approved for sickle cell disease and a related blood disorder.

Bluebird bio Inc., which nine years ago was worth nearly as much as the airline JetBlue, said it's now looking for enough ...

Stanley Joewono is an Indonesia social media influencer and exercise enthusiast. Diagnosed with thalassemia at just 8 months ...

Crispr has already secured a historic first approval for a CRISPR/Cas9 drug and has several more potential blockbuster ...

Are you planning to get a baby? Protect your child by screening for hereditary disorders that you may pass to them ...

RCCS San Raffaele Scientific Institute in Milan researchers have discovered that hematopoietic stem cells (HSCs) adapt their lineage commitment during gene therapy based on the underlying genetic ...

Pipeline candidate, exa-cel, received regulatory approval and is marketed under the name Casgevy for the treatment of sickle-cell disease (SCD) and transfusion-dependent beta-thalassemia (TDT).

Beam Therapeutics enrolls 35 patients in BEACON trial for BEAM-101 in sickle cell disease, with promising early safety and ...

Cell therapies, including CAR-T cells, and gene therapies, represent some of the forefront advancements in modern medicine. As we witness rapid technological and clinical advancements, the global ...

Thalassemia patients may also need tablets for iron chelation, a treatment for too much iron in the body. These tablets are provided free of cost at our hospitals. Currently, there is no treatment ...

He added that despite the shortage, they’ve made sure that the treatment continues and patients are receiving care. A senior official in the Union health ministry, who did not wish be to named, said a ...

Thien was diagnosed with thalassemia at nearly two years old after experiencing a high fever. He began undergoing monthly blood transfusions and iron chelation therapy at the Da Nang Maternity and ...