9-case cluster of rare pneumonia being investigated by Gaston County health officials
Public health officials are investigating a cluster of nine confirmed cases of Legionnaires’ disease among people who ...
New York Post46m
Woman with rare disease claims she’s now blind and bruised after doctors made her get 3 vaccines
A 23-year-old Florida woman has been temporarily blinded and bruised after allegedly being required to receive multiple ...
FiercePharma54m
After prior snub, Zevra clinches FDA approval for rare lysosomal storage disorder drug Miplyffa
For Zevra Therapeutics and its rare neurodegenerative disease med arimoclomol, the second time’s the charm. | The ...
US FDA approves Zevra's treatment for rare genetic disease
The U.S. Food and Drug Administration has approved Zevra Therapeutics' drug for a rare and fatal genetic disorder, making it ...
FDA Approves Zevra's Miplyffa for Niemann-Pick Disease Type C -- 2nd Update
Zevra Therapeutics has won Food and Drug Administration approval of Miplyffa for Niemann-Pick disease type C, or NPC, making it the first drug cleared in the U.S. for the rare neurodegenerative ...
'Don't shoot': Idaho Fish and Game offers advice for hunters after state confirms first case of deer plague
Washington State University pathologists confirmed Idaho's first case of plague found in a deer this week; the animal was ...
YOUR HEALTH: Emmitt’s story: From a head cold to a rare heart condition
An eight-year-old boy’s experience could be your own. He went to the doctor for head cold symptoms. He ended up in the OR to ...
Managed Healthcare Executive4h
Although Gene Therapy Offers Hope, SMA Patients Still Face Significant Health Challenges
Children with spinal muscular atrophy (SMA) experience benefits from receiving a disease-modifying gene therapy, but many ...
STAT18h
FDA approves first drug for rare neuron disease, Niemann-Pick type C
The Food and Drug Administration on Friday approved the first treatment for Niemann-Pick disease, type C, the culmination of ...
stockhead18h
The ASX stocks leading clinical trials in Australia
“The challenge for Dimerix is that we are recruiting in a rare disease population,” she said. “Australia has a relatively ...