US FDA approves Zevra's treatment for rare genetic disease
The U.S. Food and Drug Administration approved Zevra Therapeutics' drug for a rare and fatal genetic disorder, making it the ...
Psychology Today1d
How I Survived a Rare Autoimmune Disease
I walked out of my marriage and immediately fell ill. I was ill for two years. At first, I thought it was a cold that would ...
Health officials in L.A. Co. investigating rare disease spread from raccoons to humans
The Los Angeles County Department of Public Health is looking into two human cases of a rare parasitic infection that comes ...
‘Survivor 47’ preview: Terran ‘TK’ Foster on facing death’s door because of ‘pretty rare kidney disease’ [WATCH]
Survivor 47” fans, it’s time to meet Terran “TK” Foster, a 31-year-old athlete marketing manager from Upper Marlboro, ...
'One small step': Community comes together for Swansea 1-year-old with rare liver disease
A walk-a-thon fundraiser steps off in New Bedford this weekend in support of "Saige the Brave" following the 1-year-old's ...
London Man Grateful to Doctors Who Treated Rare Flesh-Eating Disease, Pledges $25,000
Despite being a flight away, Colleen's quick return home was met with relief as Dr. Alp Sener, Division Head of Urology at ...
Business Wire6h
Neu-REFIX Beta glucan receives rare pediatric disease and orphan drug designations from the US FDA for treatment of Duchenne Muscular Dystrophy
Neu refix granted orphan disease designation (ODD) & rare pediatric disease designation (RPDD) by US FDA for treatment of ...
Medpage Today on MSN6d
Gene Therapy Shows Promise in Rare Eye Disease That Causes Early Blindness
A subretinal gene therapy was well tolerated 1 year after treatment, with no drug-related serious adverse events, in a small ...
STAT17h
House panel passes pediatric rare disease bill, setting it up for government funding bill
A House committee on Wednesday passed a bill to renew a program aimed at aiding development of drugs for rare diseases in ...
FierceBiotech2d
FDA scraps adcomm for Applied's rare disease drug ahead of November decision
After pushing back the decision date for Applied Therapeutics’ metabolic disorder drug govorestat, the FDA has now decided ...
KTVQ Billings, MT on MSN12h
Calves to Cure helps fund research for rare disease battled by Worden boy
This U.S. Army film tells the story of a Japanese woman who marries an American serviceman and goes with him to the United ...
ktvq8h
Calves to Cure helps fund research for Worden boy's rare disease
The Billings Livestock Commission hosted the sixth annual Calves to Cure on Thursday, an event to help raise money and ...