A House committee on Wednesday passed a bill to renew a program aimed at aiding development of drugs for rare diseases in ...
Advocates for people with rare diseases say a government voucher program has been crucial to pursuing treatments. That ...
After pushing back the decision date for Applied Therapeutics’ metabolic disorder drug govorestat, the FDA has now decided ...
For example, this one vet chose to care for this pitbull puppy despite the fact that she had a rare and very serious disease ...
Neu refix granted orphan disease designation (ODD) & rare pediatric disease designation (RPDD) by US FDA for treatment of ...
Ongoing research is exploring new molecular targets and targeted therapies for this challenging disease.
The FDA should be more open and collaborative to unleash a surge in approvals of rare disease drugs, according to a report by ...
The Billings Livestock Commission hosted the sixth annual Calves to Cure on Thursday, an event to help raise money and ...
The Los Angeles County Department of Public Health is looking into two human cases of a rare parasitic infection that comes ...
I walked out of my marriage and immediately fell ill. I was ill for two years. At first, I thought it was a cold that would ...
The Little Giants Foundation will hold its first-ever golf tournament to raise money for research into a rare, life-limiting ...
A walk-a-thon fundraiser steps off in New Bedford this weekend in support of "Saige the Brave" following the 1-year-old's ...